As record levels of money pour into gene therapy research, biotechs are under pressure to answer questions on safety, delivery and pipelines. Discover the latest advancements in the field in this Trendline.
Gene therapy is once again at the forefront of biomedical research, catalyzed by advances in safer delivery of genes to cells. Science may also move quickly past gene replacement therapy to gene editing via CRISPR and other methods, an approach in which the unknowns are even greater and clinical results are just beginning to emerge.
INCLUDED IN THIS TRENDLINE
Sickle cell therapies’ approval marks CRISPR gene editing milestone
An oral history of the first CRISPR medicine
New CMS pilot to test payment scheme for pricey sickle cell gene therapies